Taysha Gene Therapies recently received FDA Breakthrough Therapy Designation for its Rett syndrome gene therapy TSHA-102, following encouraging REVEAL trial results and protocol alignment to enable a ...

If you’ve never heard of Rett syndrome, you’re not alone. But researchers and parents of children with Rett syndrome want to change that as they work hard for a way to reverse it. Rett syndrome is a ...

The US Food and Drug Administration has approved Acadia Pharmaceuticals’ Daybue Stix (trofinetide), a dye and ...

With strong 1-year returns and upside potential, Taysha Gene Therapies, Inc. (NASDAQ:TSHA) secures a spot on our list of the ...

ALMA --Becca Loney befriended Siera Rushin, and it wasn't long before the two girls were watching videos, heading to parties and dances and planning to go to the prom. Siera, 20, has Rett syndrome, a ...

An expert discusses the current treatment landscape of Rett syndrome including the goals of treatment and implications for utilization management strategies with the disease. David Lieberman, MD, PhD: ...

In the comfort of her Miami home, 34-year-old Julianne Espinosa lies in bed captivated by videos of Disney princesses flashing across her television screen. As echoes of “The Little Mermaid” fill her ...

What is Rett syndrome and why does it affect only girls? Rett syndrome is a rare neurological disorder that causes victims to regress intellectually, gradually robbing their ability to think and move.

Paige Nues provides her closing thoughts regarding the treatment management of Rett syndrome. Paige Nues: We have never felt more optimistic than [at] any time in the Rett syndrome’s history in terms ...

The JR Group’s Glasgow charity gala raised £170,000 for Reverse Rett, supporting Rett Syndrome research, with top auction ...

Richard Engel calls it the worst day of his life. The chief foreign correspondent for NBC News was with U.S. troops in South Korea when he received the results of a genetic scan for his sweet young ...